CRANBURY, N.J.--(BUSINESS WIRE)--Jun. 28, 2024-- Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company...
Vous n'êtes pas connecté
Per the FDA, Rocket (RCKT) needs to submit additional manufacturing information on Kresladi gene therapy to secure approval for severe leukocyte adhesion deficiency-I (LAD-I), a rare genetic disorder.
CRANBURY, N.J.--(BUSINESS WIRE)--Jun. 28, 2024-- Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company...
MONDAY, June 24, 2024 -- The U.S. Food and Drug Administration has expanded the approval of Elevidys (delandistrogene moxeparvovec-rokl), a gene...
CAMBRIDGE, Mass.--(BUSINESS WIRE)--Jun. 20, 2024-- Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare...
Falling rocket debris in China after launches is not unheard of, but it is very rare for part of a rocket under development to make an unplanned...
Falling rocket debris in China after launches is not unheard of, but it is very rare for part of a rocket under development to make an unplanned...
In 2019, scientists identified a Colombian woman who, as a result of her genes, should have experienced symptoms of Alzheimer’s disease starting in...
Eli Lilly's (LLY) Alzheimer's disease drug, Kisunla (donanemab), wins FDA approval. Kisunla will be the second drug on the market to treat the...
The post
BASKING RIDGE, N.J. & RAHWAY, N.J., June 26, 2024 – The U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL)...
New clinical test detects Calcium Release Deficiency Syndrome (CRDS), a genetic arrhythmia with rapid heartbeats leading to sudden cardiac arrest.