Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude Children's Research...

Discover the first in-utero treatment for spinal muscular atrophy (SMA) using risdiplam. Promising results show no SMA signs in a child two years...

TUESDAY, Feb. 18, 2025 -- The U.S. Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for...

A two-and-a-half-year-old girl was successfully treated for a rare genetic motor neuron disease. In a groundbreaking study, the patient began...

South San Francisco, CA -- February 12, 2025 -- Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), announced today that the U.S....

The World Health Organization (WHO) and St. Jude Children's Research Hospital have commenced distribution of critically-needed childhood cancer...

Researchers at the University of Hong Kong’s LKS Faculty of Medicine (HKUMed) have developed an oral form of arsenic trioxide (Oral-ATO;...

GENEVA, Switzerland – The World Health Organization (WHO) and St Jude Children’s Research Hospital have commenced distribution of...

Indian scientists have made a major advancement in medlinkRheumatoid Arthritis/medlink treatment with a groundbreaking b"self-actuating"/b drug...

Up to half of all people living with Alzheimer’s Disease in Ireland remain undiagnosed. Now, a new blood test may have the potential to transform...