Highlights: 62 ADA SCID infants treated in the largest long-term study to date 95 percent developed durable immu

In preclinical studies, researchers found that priming the immune system with a Treg-expanding therapy before stem cell transplant boosted survival,...

“Bubble boy disease” was once a death sentence. A scientific breakthrough changed that.

The launch of BIRSA 101 marks a major breakthrough in CRISPR gene-editing technology, positioning India to deliver affordable cures for Sickle Cell...

ABU DHABI, 27th November, 2025 (WAM) — Yas Clinic – Khalifa City, in collaboration with the Abu Dhabi Stem Cells Centre (ADSCC) and Vertex...

In preclinical studies, researchers found that priming the immune system with a Treg-expanding therapy before stem cell transplant boosted survival,...

A three-year-old Oliver (Ollie) Chu has become the world’s first patient to receive a revolutionary stem cell gene therapy for Hunter syndrome. ...

A three-year-old Oliver (Ollie) Chu has become the world’s first patient to receive a revolutionary stem cell gene therapy for Hunter syndrome. ...

Hunter Syndrome (MPSII) is a rare disease but the sufferer will slowly die before the age of 20. It occurs once in every 100,000 male births and...

Hunter Syndrome (MPSII) is a rare disease but the sufferer will slowly die before the age of 20. It occurs once in every 100,000 male births and...