Kendric Cromer, 12, is among the first patients to be treated with gene therapy just approved by the F.D.A. that many other patients face obstacles to...

Kendric Cromer, 12, is among the first patients to be treated with gene therapy just approved by the F.D.A. that many other patients face obstacles to...

Researchers at the National Institutes of Health (NIH) have revealed that carriers of sickle cell disease, known as having sickle cell trait, are at...

Being a carrier of sickle cell disease raises the risk of blood clots across diverse populations, according to NIH research.

THURSDAY, Sept. 5, 2024 -- Lung function remains stable over three years after hematopoietic cell transplant (HCT) among patients with sickle cell...

FRIDAY, Sept. 6, 2024 -- Gene therapy may restore vision to children and adults robbed of their sight by a rare inherited condition called Leber...

After a single gene therapy treatment, patients with genetic blindness experienced new visual moments.

After a single gene therapy treatment, patients with genetic blindness experienced new visual moments.

Patients born with genetic blindness experienced significant visual improvements after a single treatment with gene therapy developed at the...

Patients born with genetic blindness experienced significant visual improvements after a single treatment with gene therapy developed at the...